Research Updates

Huntington’s disease goes viral as UniQure inches ahead in gene therapy race

This information is provided from a recent blog published by HDBuzz. To view more of their articles or subscribe directly to news published by HDBuzz you can find more information on their website: www.en.hdbuzz.net/ By Dr Jeff Carroll   January 29, 2019    Edited by Dr Ed Wild Dutch-American company uniQure has received approval from the US drug regulator the FDA, to begin the first ever gene therapy trial in Huntington’s Disease. Their

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Is CRISPR the future of HD treatment?

As the current work by WAVE Life Sciences and IONIS/Roche into Huntingtin Lowering Therapy (gene silencing) unfolds and we wait for the outcome of clinical trials, scientists are already working on new technologies that might treat Huntington’s Disease. One of those is called CRISPR; it is a method for cutting

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A cautious welcome for the latest results from IONIS Phase One Trial

So, after posting an article this morning about the inevitable lull since IONIS released the results of its phase one trial, they have now issued a press release providing additional results from their analysis of the phase one study. You can see it by following this link http://ir.ionispharma.com/news-releases/news-release-details/new-data-ionis-htt-rx-phase-12-study-demonstrates-correlation Let’s do a

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A wave of new ideas?

There has been a great deal of focus over the last few months on the work of IONIS pharmaceuticals who are developing a gene silencing drug (currently known as IONIS HTTrx); this is largely because they were the first to complete a successful phase one clinical trial and announce very

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